“When my brother Ryan was diagnosed with Duchenne muscular dystrophy, our world changed forever. As his primary caretaker for over a decade, I experienced firsthand the heartbreak of watching him face the relentless progression of this disease- but also the extraordinary moments of resilience, joy, and unwavering hope that defined his spirit. It was this journey that led to the founding of our organization, built on a mission to fight for better treatments, better care, and a better future for families like ours. This year, we reached a milestone that once felt like a distant dream: the launch of the first FDA approved mesenchymal stem cell clinical trial for DMD. It was a founding goal, one that Ryan and I spoke about countless times, and seeing it come to life is deeply personal. ”
“Looking forward, we are firmly committed to growing our partnerships and significantly increasing the quality of care available to our community. The gaps we’ve identified in the current support ecosystem require innovative solutions and collaborative approaches, which will be our priority in the coming year.”
